Health ❯Medical Research

Gene Therapy

Personalized Medicine Ophthalmology Quality Control CRISPR Applications RNA Interference CRISPR Technology Inherited Conditions Viral Vectors siRNA Therapy MicroRNA Applications mRNA Technology Gene Manipulation MicroRNA Treatments Targeted Therapy Adeno-Associated Virus (AAV) mRNA Vaccines AFM-Téléthon Sickle Cell Disease Heart Failure Cardiovascular Health Epigenetic Editing Duchenne Muscular Dystrophy OTOF Gene OTOF Gene Therapy AAV Vectors Acoustic Stimulation Genetic Disorders Hearing Restoration Antisense Oligonucleotides Clinical Trials

evoCAST Gene Editor Achieves Breakthrough in Precision DNA Insertion

Published in Science, the lab-evolved system achieves 30–40% efficiency in inserting complete genes into human cells, with potential for universal gene therapies but delivery challenges remain.

UCSF Research Advances Prenatal Therapy for Spinal Muscular Atrophy

Federal Court Orders Reconsideration of CRISPR Patent Priority Decision

Kyoto University Study Reveals Cells Directly Respond to Sound Waves

Gene Therapy Reverses Heart Failure in Groundbreaking Animal Study

Engineers Develop Faster, Safer Lipid Nanoparticles for mRNA Therapies

AI-Engineered DNA Switches Enable Precise Gene Control in Specific Cells

Innovative Nanoparticles Enhance Precision in mRNA and siRNA Therapies

New Genetic Tool Shows Promise in Treating High Cholesterol

Breakthrough Gene Therapies Offer New Hope for Sickle Cell Disease

Gene Therapy Shows Promise in Restoring Vision for Patients with Rare Genetic Disorder

Gene Therapy Shows Dramatic Vision Restoration in Rare Eye Condition

Gene Therapy Restores Hearing in Children with Hereditary Deafness

Gene Therapy Successfully Restores Hearing in Children with Hereditary Deafness